Rare Care School of Medicine news release | Division of Genetics & Genomic Medicine

WashU Medicine launches center for rare diseases (Links to an external site)

February 14, 2025March 5, 2025

Featured image from linked article

New effort unites vast rare disease network to advance research, therapies.

Fatal neurodegenerative disease in kids also affects the bowel (Links to an external site)

January 15, 2025March 7, 2025

Jonathan Cooper, PhD, left, postdoctoral research associate Ewa Ziółkowska, PhD, and Matt Jensen go over data from their paper. Cooper and his lab study Batten disease in the McDonnell Pediatric Research Building on November 19, 2024. MATT MILLER/WASHINGTON UNIVERSITY SCHOOL OF MEDICINE

Gene therapy, in mice modeling Batten disease, found to slow symptoms, extend lifespan